Jesse Gelsinger died after receiving a gene therapy treatment to treat a liver disease. The death sparked an investigation ...

The indication has been expanded to include use in newborns and allows patients and caregivers to apply the treatment at home ...

At the European Cell & Gene Therapy Summit 2025, funding challenges and innovation drove discussions on the sector’s future.

A new analyst survey suggests that doctors are still prescribing Sarepta’s Elevidys, even after a series of deaths in certain ...

Prominent critics say Sarepta’s Elevidys Duchenne therapy may overstate how much gene it delivers—raising new questions about ...

Sangamo Therapeutics hasn’t convinced a pharma company to buy its experimental gene therapy for Fabry disease after two years ...

The commercial success of existing lipid-lowering medications highlights the enormous market potential for effective ...

The biotech has paused its Phase I trial of CAP-002, pending investigation into the “root cause” of the death.

The medium, which is designed for high density perfusion culture, is available in a variety of media package options for continuous processing.

Roni Hahn & Prof. Karen Avraham. Scientists from the Gray Faculty of Medical & Health Sciences at Tel Aviv University ...

Capsida is investigating the root cause of the death, which occurred in the first patient treated in a trial of the company’s ...