Across 100 patients in three Phase III studies, Vertex's Casgevy showed lasting benefits for more than five years.

A 7-year-old girl completely restored her hearing and began to speak freely just four months after the treatment, maintaining ...

Abu Dhabi (DoH), the regulator of the healthcare sector in Abu Dhabi, has announced a landmark partnership with the ...

A researcher says an experimental gene therapy for a rare inherited disorder is saving almost as much money for the treatment ...

A breakthrough gene therapy has helped restore hearing in both children and adults with a genetic form of deafness or severe ...

Prof AK Sood emphasizes the need for affordable cell and gene therapies in India, highlighting the current challenges and the ...

Sarepta is facing a shareholder lawsuit over ELEVIDYS-related deaths. Robbins LLP cites safety risks and stock losses.

One-time surgical application of genetically engineered autologous keratinocyte sheets provides significant closure and pain ...

A first-of-its-kind trial shows gene therapy can successfully restore hearing in adults and toddlers with OTOF-related congenital deafness.

A single jab of a breakthrough gene therapy could reverse hearing loss in people within weeks, according to new research.