A breakthrough gene therapy has helped restore hearing in both children and adults with a genetic form of deafness or severe ...

A single jab of a breakthrough gene therapy could reverse hearing loss in people within weeks, according to new research.

A researcher says an experimental gene therapy for a rare inherited disorder is saving almost as much money for the treatment ...

A new study shows that gene therapy can significantly improve hearing in both children and adults with congenital deafness ...

A new gene therapy has shown promising results in restoring hearing to children, teens, and even a young adult born with a ...

Gene therapy can improve hearing in children and adults with congenital deafness or severe hearing impairment, a new study ...

A new gene therapy trial safely restores hearing in deaf children and adults, offering hope for those with DFNB9 deafness ...

Gene therapy has been effective for young children with genetic hearing loss, but this is the first study to show promising ...

This is the first time such results have been achieved in both children and adult patients born with a specific type of ...

Pompe's disease is a lysosomal storage disorder caused by a genetic deficiency of GAA. The disease is associated with severe ...

A new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a wholesale price of $4.25 million, its manufacturer announced Wednesday, making it the world’s ...

We look at the continued turmoil within the FDA, including the forced dismissal of top gene therapy regulator Nicole Verdun, ...