Please provide your email address to receive an email when new articles are posted on . Severe auditory dysfunction was a common neurobiological feature of neurofibromatosis type 1, according to ...
Plexiform neurofibromas (PN) are a common type of tumor in children with neurofibromatosis type 1 (NF1) that can cause a variety of symptoms and complications. Learning more about treatment options ...
A Montgomery County family is turning heartbreak into purpose after losing their 17-month-old daughter, Mila Roomberg. Mila had a rare condition — and an even rarer complication: dangerously high ...
GOMEKLI is the first FDA-approved treatment for adult and pediatric NF1-PN, showing effective tumor reduction and manageable safety. SpringWorks Therapeutics has announced the FDA approval of GOMEKLI ...
Almost half of adults and children with neurofibromatosis type 1 (NF1) responded to the investigational MEK inhibitor mirdametinib, a large multicenter study of the rare condition showed. Overall, 53 ...
Neurofibromatosis type 1 (NF1) is the most common of the three types of neurofibromatosis and is also one of the most common inherited neurological disorders, affecting about 1 in 3,000 people ...
Treatment for neurofibromatosis type 1 may involve surgery, radiation therapy, or medication. In some cases, treatment may not be necessary unless symptoms become bothersome. Neurofibromatosis type 1 ...
Selumetinib received FDA approval for adults with NF1 and symptomatic, inoperable plexiform neurofibromas, based on the phase 3 KOMET trial results. The KOMET trial showed a 20% objective response ...
Neurofibromatosis type 1 (NF1) is a genetic condition that affects the skin, nervous system, and other parts of the body. The condition, formerly called Von Recklinghausen disease, causes changes in ...